This is the power of progress. The power of community. The power of science driven by compassion.
Gene therapy is rewriting futures for kids like Jacob. Just six weeks after he was born, Jacob was diagnosed with Spinal Muscular Atrophy Type 1- a condition once considered a heartbreaking, life-limiting diagnosis. But today, he is a thriving, joyful one-year-old who adores toy cars and playing outside. His transformation is nothing short of extraordinary, and it’s all thanks to gene therapy.
“The things that Jacob is doing now because of gene therapy are just unbelievable,” says his mum, Brooke.
For families like Jacob’s, advanced therapies offer not just hope – but a future filled with possibilities. Jacob now spends more time exploring the world outside hospital walls, and Brooke proudly shares that the treatment is doing what once felt impossible.
“Now we’re aiming to get Jacob to walk – something that, just a decade ago, wasn’t even a dream for children with SMA.